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Substrate reduction using N-butyldeoxynojirimycin (OGT 918): Clinical trial of a novel oral therapy for Gaucher´s disease
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Gaucher disease01
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MUDr. Martin Hřebíček Ph.D.
First Faculty of Medicine
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R. H. Lachmann
Person without faculty affiliation
person
C. E. M. Hollak
Person without faculty affiliation
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J. M. F. G. Aerts
Person without faculty affiliation
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S. van Weely
Person without faculty affiliation